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level to affected muscle cells. Dosage, as well as a viable means for systemic release of the drug in patients, is currently being investigated with the use of both
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is the underlying defect responsible for both disorders, biostrophin will deliver a genetically-engineered, functional copy of the gene at the
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Biostrophin is being manufactured by
Asklepios BioPharmaceuticals, Inc., with funding provided by the
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Please help update this article to reflect recent events or newly available information.
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Khurdayan VK, Bozzo J, Prous JR (Oct 2005). "Chronicles in drug discovery".
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